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Delhi HC exempts custom duties on medicines for rare diseases
The Delhi High Court has said that custom duties and charges will not be applied to medicines, drug…
Sarepta tumbles after the FDA rejects its muscular dystrophy treatment - a decision that left the CEO 'very surprised'
The company's first drug for Duchenne muscular dystrophy was approved in 2016 after prolonged debat…
Ben Winck
Govt waives clinical trial requirement for several drugs approved in select countries
This waiver would ensure expeditious availability of the latest medicines for treating diseases …
PTI
Centre gives full basic customs duty exemption on import of drugs for rare diseases
In a significant step, the Centre has given full exemption from basic customs duty on all drugs as …
5L patients of rare disease, treatment costs in crores; govt lacks budget: HC told
The court had earlier asked the ministry to write to the company -- Sarepta Therapeutics in USA -- …
PTI
Sarepta Therapeutics spikes 57% after a key trial shows its experimental gene therapy worked in 3 patients
"I have been waiting my entire 49-year career to find a therapy that dramatically reduces CK levels…
Jonathan Garber,Lydia Ramsey
Some patients say a commonly prescribed steroid triggered mania and suicidal ideation. I should know — it happened to me.
Prednisone is prescribed to millions of Americans. While mood swings are a known side effect, some …
Julia Métraux
An old steroid used to treat a rare disease just got approved by the FDA - and it costs $89,000
The move is reminiscent of a plan former pharma CEO Martin Shkreli had with a treatment for another…
Lydia Ramsey,Reuters
Another controversial drugmaker just left the industry's most powerful lobby
PhRMA has made a point of distinguishing itself from companies that have drawn outrage about drug p…
Lydia Ramsey
Biotech stock explodes 80% after the FDA approves the first drug to treat a rare muscle disorder
"Accelerated approval makes this drug available to patients based on initial data, but we eagerly a…
Akin Oyedele
Biotech stock crashes 50% after disclosing bad news from the FDA
"The advisory committee voted 3 - 7, with three abstentions, against finding substantial evidence b…
Akin Oyedele
Over 1,500 federal workers affected by the government shutdown are asking for donations on GoFundMe to help pay their bills
Nikolai, Niko for short, has Muscular Dystrophy Duchenne, a disease that left him wheelchair-bound,…
Mariana Alfaro
STOCKS GO NOWHERE: Here's what you need to know
An early rally in West Texas Intermediate crude futures also fizzled out. Venezuelan President Nico…
Akin Oyedele
This stainless steel wristwatch just became the most expensive ever sold
The model is a variation on Patek Phillipe's 5016 model, except that it's made with a stainless ste…
Dennis Green
Congress is going after another drugmaker for pricing a decades-old drug at $89,000
"We believe Marathon is abusing our nation's "orphan drug" program, which grants companies seven ye…
Lydia Ramsey
Biotech Stock Crashes After FDA Requires Additional Data For New Drug Application
In a statement Chris Garabedian, president and CEO of Sarepta Therapeutics said: "We are committed …
Myles Udland
Paramount Goes Above And Beyond To Help A Sick 'Teenage Mutant Ninja Turtles' Fan
What a spectacular trend this has become. Do you recall, recently, when Marvel went out of its way …
Sean O'Connell
10 things you need to know before European markets open
Brits are holding more and more cash, and it is a worrying sign for the UK's post-Brexit economy, a…
Will Martin
LeBron James sent a heartfelt letter to a 19-year-old with a terminal illness
I've heard some pretty amazing things about you, and from what I've heard, I can tell you are an un…
Scott Davis
Sarepta Is Surging After Good News For Its Ebola Treatment
AVI-6002 for the treatment of Ebola is a combination therapy of two phosphorodiamidate morpholino o…